What Are the RASopathies?

 
 

Learn about the individual RASopathy syndromes

 
 

1:1,000 ?

Individually, each of the RASopathies is rare ~ Together they come close to 1:1,000

 
 

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Clinicians around the world

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Latest News

Suspension of BioMarin Clinical Trial of VOXZOGO® (vosoritide) in Noonan Syndrome

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BioMarin has made the decision to discontinue development of VOXZOGO® (vosoritide) for children with Noonan syndrome. Read the press release here.

Molecular Glue

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Restoring the brake: Using molecular glues to fix a broken CRAF off-switch in Noonan Syndrome   Another RAS Dialogue Blog post has dropped from the NCI Frederick National Lab RAS…

Advancing RAS/RASopathies Therapies

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❓ What have we been working towards? ♥ Read the RAS Dialogue Blog from Marielle Yohe that encapsulates the efforts of so many people who care about and want to…

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